(1) Registry of Members of The Association of Patients With Hereditary Angioedema of Perú

Oscar Calderón Llosa

Oscar Calderón Llosa1, Danny Muñoz Campos2, Margarita Olivares Gómez3

  1. Angioedema Center of Reference and Excellence-ACARE, Clínica SANNA el Golf, San Isidro, Lima, Perú
  2. Angioedema Center of Reference and Excellence-ACARE, Clínica SANNA el Golf, San Isidro, Lima, Perú
  3. Clínica Medellín Poblado; Unidad Alergológica. Medellín, Colombia

(2) Early-Onset Response to the Oral Bradykinin B2 Receptor Antagonist Deucrictibant Immediate-Release Capsule in Patients with Hereditary Angioedema Attacks

Marcus Maurer

Marcus Maurer1,2, John Anderson3, Emel Aygören-Pürsün4, Danny M. Cohn5, Henriette Farkas6, H. Henry Li7, Markus Magerl1,2, Rafael Crabbé8, Li Zhu9, Peng Lu9, Giorgio Giannattasio10, Marc A. Riedl11

  1. Institute of Allergology, Charité – Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin, Germany
  2. Fraunhofer Institute for Translational Medicine and Pharmacology ITMP, Allergology and Immunology, Berlin, Germany
  3. AllerVie Health, Clinical Research Center of Alabama, Birmingham, AL, United States
  4. University Hospital Frankfurt, Department for Children and Adolescents, Goethe University Frankfurt, Frankfurt, Germany
  5. Amsterdam Cardiovascular Sciences, Amsterdam UMC, Department of Vascular Medicine, University of Amsterdam, Amsterdam, The Netherlands
  6. Hungarian Angioedema Center of Reference and Excellence, Department of Internal Medicine and Haematology, Semmelweis University, Budapest, Hungary
  7. Institute for Asthma and Allergy, Chevy Chase, MD, United States
  8. RC Consultancy, Bassins, Switzerland
  9. Pharvaris Inc, Lexington, MA, United States
  10. Pharvaris GmbH, Zug, Switzerland
  11. University of California San Diego, Division of Rheumatology, Allergy and Immunology, La Jolla, CA, United States

(3) Registry of Members of the Association of Patients with Hereditary Angioedema in the Republic of Panama

Olga M. Barrera

Olga M. Barrera1, Marisela Williams2, Georgina Díaz3, Dayanara Herrera4, Janina Vergara5, Diva Almillategui5, Manuel Cruz6, Manuel Espinoza7, Indira Santos8

  1. San Fernando Hospital, INASA, Panama
  2. Pediatric Specialties Hospital, Panama
  3. Allergic Private Clinical, Santiago, Panama
  4. Pediatric Specialties Hospital, Panama
  5. Children´s Hospital of Panama, Panama
  6. Dr Chicho Fabrega Hospital, Social Security, Santiago, Panama
  7. Chiriqui Hospital, David, Panama
  8. International Maritime University of Panama, Panama

(4) Efficacy and Safety of the Oral Bradykinin B2 Receptor Antagonist Deucrictibant Immediate-Release Capsule in Treatment of Hereditary Angioedema Attacks: RAPIDe-3 Phase 3 Trial Design

Anete S. Grumach

Anete S. Grumach1, John Anderson2, Mauro Cancian3, Danny M. Cohn4, Henriette Farkas5, Atsushi Fukunaga6, Michihiro Hide7, Constance H. Katelaris8, Philip H. Li9, William R. Lumry10, Markus Magerl11,12, Marc A. Riedl13, Ricardo D. Zwiener14, Ming Yu15, Raf Crabbé16, Eivind Omli17, Li Zhu15, Joan Mendivil18, Peng Lu15, Marcus Maurer11,12

  1. Clinical Immunology, Centro Universitario FMABC, Sao Paulo, Brazil
  2. Clinical Research Center of Alabama, AllerVie Health Birmingham, AL, United States
  3. Department of Systems Medicine, University Hospital of Padua, Padua, Italy
  4. Department of Vascular Medicine, Amsterdam Cardiovascular Sciences, Amsterdam UMC, University of Amsterdam, Amsterdam, The Netherlands
  5. Department of Internal Medicine and Haematology, Hungarian Angioedema Center of Reference and Excellence, Semmelweis University, Budapest, Hungary
  6. Division of Dermatology, Department of Internal Related, Kobe University Graduate School of Medicine, Chuo-ku, Kobe, Japan and Department of Dermatology, Division of Medicine for Function and Morphology of Sensory Organs, Faculty of Medicine, Osaka Medical and Pharmaceutical University, Takatsuki, Osaka 569-8686, Japan
  7. Department of Dermatology, Hiroshima University and Hiroshima Citizens Hospital, Hiroshima, Japan
  8. Department of Medicine, Campbelltown Hospital and Western Sydney University, Sydney, New South Wales, Australia
  9. Division of Rheumatology and Clinical Immunology, Department of Medicine, Queen Mary Hospital, University of Hong Kong, Hong Kong
  10. Internal Medicine, Allergy Division, University of Texas Health Science Center, Dallas, TX, United States
  11. Institute of Allergology, Charité – Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin, Germany
  12. Fraunhofer Institute for Translational Medicine and Pharmacology ITMP, Immunology and Allergology, Berlin, Germany
  13. Division of Rheumatology, Allergy and Immunology, University of California San Diego, La Jolla, CA, United States
  14. Servicio de Alergia e Inmunología, Hospital Universitario Austral, Buenos Aires, Argentina
  15. Pharvaris Inc., Lexington, MA, United States
  16. RC Consultancy, Bassins, Switzerland
  17. Pharvaris Netherlands BV, Leiden, The Netherlands
  18. Pharvaris GmbH, Zug, Switzerland

(5) Anxiety Associated with Refilling On-demand Therapy for HAE Attacks Contributes to Treatment Delay and Non-Treatment

Anete S. Grumach

Daniel F. Soteres1, Anete S. Grumach2, Autumn Burnette3

  1. University of Colorado Health Sciences Center, Denver, Colorado, United States
  2. Center of Reference for Rare Diseases, Faculdade de Medicina ABC, São Paulo, Brazil
  3. Howard University, Washington, DC, United States

(6) HAE attacks in Canadian Patients with HAE: Triggers and Treatment Based on Data From the 2020 National Survey

Jacquie Badiou

Jacquie Badiou1, Michelle Cooper1, Daphne Dumbrille1, Suzanne M. Kelly2, Paul K. Keith3, Amin Kanini4, Chrystyna Kalicinsky5, William H. Yang2,6

  1. Hereditary Angioedema Canada
  2. Red Maple Trials Inc, Ottawa, ON, Canada
  3. McMaster University, Hamilton, ON, Canada
  4. University of British Columbia, Vancouver, BC, Canada
  5. University of Manitoba, Winnipeg, MB, Canada
  6. University of Ottawa, Ottawa, ON, Canada

(7) Characterizing the Negative Impact of Delayed On-Demand Treatment of HAE Attacks

Ricardo Zwiener

Princess Ogbogu1, Hilary Longhurst2, Ricardo Zwiener3

  1. Case Western Reserve University School of Medicine, Cleveland, Ohio, United States
  2. Te Toka Tumai, Auckland City Hospital, New Zealand
  3. Hospital Universitario Austral, Buenos Aires, Argentina

(8) Characterization of Prodromes in Hereditary Angioedema: Findings From an Online Patient Forum

Marc A. Riedl

Marc A. Riedl1, Lindsey Noble2, Tamara Ray2, Douglas T. Johnston2, Clare Murphy3, Henry Li4

  1. Division of Rheumatology, Allergy, and Immunology, University of California San Diego, La Jolla, CA, United States
  2. Biocryst Pharmaceuticals, Inc., Durham, NC, United States
  3. KJT Group, Inc, Rochester, NY, United States
  4. Institute for Allergy and Asthma, Chevy Chase, MD, United States

(9) Characteristics of Hereditary Angioedema Attacks Among Long-Term Prophylaxis Users

Maeve O’Connor

Bob Geng1, Vibha Desai2, Julie Ulloa3, Sherry Danese3, Paul Audhya2, Timothy Craig4

  1. Allergy and Immunology, University of California, San Diego, California, United States
  2. KalVista Pharmaceuticals, Cambridge, MA, United States
  3. Outcomes Insights, Agoura Hills, CA, United States
  4. The Pennsylvania State University School of Medicine, State College, PA, United States

(10) Delayed On-demand Treatment of Hereditary Angioedema Attacks: Patient Perceptions and Associated Barriers

Maeve O’Connor

Sandra Christiansen1, Maeve O’Connor2, Julie Ulloa3, Sherry Danese3, Vibha Desai4, Paul Audhya4, Paula Busse5

  1. University of California San Diego, La Jolla, CA, United States
  2. Allergy Asthma and Immunology Relief of Charlotte, Charlotte, NC, United States
  3. Outcomes Insights, Agoura Hills, CA, United States
  4. KalVista Pharmaceuticals, Cambridge, MA, United States
  5. The Mount Sinai Hospital, New York, NY, United States

(11) Findings and Insights from a Colombian National Survey on Hereditary Angioedema due to C1-inhibitor deficiency

Margarita Olivares-Gomez

Margarita Olivares-Gomez1

  1. Clínica Medellín Poblado, Universidad de Antioquia. Medellín, Colombia

(12) Treatment Patterns of Patients Requiring Redosing of an On-demand Treatment After the Return of an HAE Attack

William Lumry

Constance Katelaris1, Michael Manning2, William Lumry3

  1. Western Sydney University and Campbelltown Hospital, New South Wales, Australia
  2. UA College of Medicine-Phoenix, Phoenix, AZ, United States
  3. University of Texas Southwestern Medical School, Dallas, TX, United States

(13) Efficacy and Safety of Bradykinin B2 Receptor Antagonism with Deucrictibant Immediate-Release Capsule for Treatment of Hereditary Angioedema Attacks: Results of RAPIDe-1 Phase 2 Trial

Markus Magerl

Markus Magerl1,2, John Anderson3, Emel Aygören-Pürsün4, Maria Luisa Baeza5, Laurence Bouillet6, Hugo Chapdelaine7, Danny M. Cohn8, Aurélie Du-Thanh9, Olivier Fain10, Henriette Farkas11, Jens Greve12, Mar Guilarte13, David Hagin14, Roman Hakl15, Joshua S. Jacobs16, Aharon Kessel17, Sorena Kiani-Alikhan18, Pavlina Králícková19, H. Henry Li20, Ramon Lleonart21, Michael E. Manning22, Avner Reshef23, Marc A. Riedl24, Bruce Ritchie25, Giuseppe Spadaro26, Maria Staevska27, Petra Staubach28, Marcin Stobiecki29, Gordon L. Sussman30, Michael D. Tarzi31, Anna Valerieva27, William H. Yang32, Marie-Helene Jouvin33, Rafael Crabbé34, Simone van Leeuwen35, Huaihou Chen33, Li Zhu36, Jochen Knolle37, Anne Lesage38, Peng Lu36, Marcus Maurer1,2

  1. Charité – Universitätsmedizin Berlin, Institute of Allergology, Corporate Member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin, Germany
  2. Fraunhofer Institute for Translational Medicine and Pharmacology ITMP, Immunology and Allergology, Berlin, Germany
  3. AllerVie Health, Clinical Research Center of Alabama, Birmingham, AL, United States
  4. University Hospital Frankfurt, Department for Children and Adolescents, Goethe University Frankfurt, Frankfurt, Germany
  5. Hospital General Universitario Gregorio Marañón, Biomedical Research Network on Rare Diseases-U761, Institute for Health Research, Allergy Department, Gregorio Marañón, Madrid, Spain
  6. National Reference Center for Angioedema (CREAK), Department of Internal Medicine, Grenoble Alpes University, Laboratoire T-RAIG, UMR 5525 TIMC-IMAG (UGA-CNRS), Grenoble, France
  7. CHU de Montréal, Université de Montréal, Montréal, QC, Canada
  8. Amsterdam Cardiovascular Sciences, Amsterdam UMC, Department of Vascular Medicine, University of Amsterdam, Amsterdam, The Netherlands
  9. University Montpellier, Department of Dermatology, Montpellier, France
  10. Sorbonne University, Department of Internal Medicine, AP-HP, Saint Antoine Hospital, Paris, France
  11. Hungarian Angioedema Center of Reference and Excellence, Department of Internal Medicine and Haematology, Semmelweis University, Budapest, Hungary
  12. Ulm University Medical Center, Department of Otorhinolaryngology, Head and Neck Surgery, Ulm, Germany
  13. Universitari Vall d’Hebron, Allergy Section, Internal Medicine Department, Hospital Barcelona, Spain
  14. Tel Aviv Sourasky Medical Center and Sackler Faculty of Medicine, Allergy and Clinical Immunology Unit, Department of Medicine, University of Tel Aviv, Tel Aviv, Israel
  15. St. Anne’s University Hospital in Brno and Faculty of Medicine Department of Clinical Immunology and Allergology, Masaryk University, Brno, Czech Republic
  16. Allergy and Asthma Clinical Research, Walnut Creek, CA, United States
  17. Technion-Israel Institute of Technology, Bnai Zion Medical Center, Haifa, Israel
  18. Royal Free London NHS Foundation Trust, Department of Immunology, London, United Kingdom
  19. University Hospital Hradec Kralove, Institute of Clinical Immunology and Allergy, Charles University, Faculty of Medicine in Hradec Kralove, Hradec Kralove, Czech Republic
  20. Institute for Asthma and Allergy, Chevy Chase, MD, United States
  21. Bellvitge University Hospital, Allergology Service, L’Hospitalet de Llobregat, Barcelona, Spain
  22. Allergy, Asthma and Immunology Associates, Ltd., Scottsdale, AZ, United States
  23. Barzilai University Hospital, Allergy, Immunology and Angioedema Center, Ashkelon, Israel
  24. University of California San Diego, Division of Rheumatology, Allergy and Immunology, La Jolla, CA, United States
  25. Division of Hematology, Department of Medicine, University of Alberta, Edmonton, AB, Canada
  26. University of Naples Federico II, Department of Translational Medical Sciences and Center for Basic and Clinical Immunology Research (CISI), Napoli, Italy
  27. University Hospital “Alexandrovska”, Department of Allergology, Clinic of Allergology, Medical University of Sofia, Sofia, Bulgaria
  28. University Medicine Mainz, Department of Dermatology, Mainz, Germany
  29. Jagiellonian University Medical College, Department of Clinical and Environmental Allergology, Krakow, Poland
  30. Gordon Sussman Clinical Research Inc, Toronto, ON, Canada
  31. Brighton and Sussex Medical School, Department of Medicine, Brighton, United Kingdom
  32. Ottawa Allergy Research Corporation, Department of Medicine, University of Ottawa, Ottawa, ON, Canada
  33. Former employee of Pharvaris Inc., Lexington, MA, United States
  34. RC Consultancy, Bassins, Switzerland
  35. SLC Consultancy, Woerden, The Netherlands
  36. Pharvaris Inc., Lexington, MA, United States
  37. JCK Consult, Frankfurt, Germany
  38. GrayMatters Consulting, Schilde, Belgium

(14) Anxiety Associated with On-Demand Treatment for Hereditary Angioedema Attacks

Sandra Christiansen

James Wedner1, Cristine Radojicic2, Julie Ulloa3, Sherry Danese3, Vibha Desai4, Paul Audhya4, Sandra Christiansen5

  1. Washington University School of Medicine, St Louis, MO, United States
  2. Duke University School of Medicine, Durham, NC, United States
  3. Outcomes Insights, Agoura Hills, CA, United States
  4. KalVista Pharmaceuticals, Cambridge, MA, United States
  5. University of California San Diego, La Jolla, CA, United States

(15) Diagnosis and Treatment of Patients with Hereditary Angioedema in Cuba

Consuelo Macias

Consuelo Macias1, Catalino Ustariz1, Lay Salazar2, Yaxunaris Pérez1, Maria de los Angeles Garcia1, Odalys Orraca3, Vianed Marsán1, Julio César Merlín1, Rinaldo Villaescusa1, Adita Arce1, Belkis Usilora4, Osmel Guerra5

  1. Institute of Hematology and Immunology, Cuba
  2. Villa Clara Immunology Group, Cuba
  3. Pinar del Río Immunology Group, Cuba
  4. Santiago de Cuba Immunology Group, Cuba
  5. Guantánamo Immunology Group, Cuba